Neuronopathic Gaucher's disease: Induced pluripotent stem cells for disease modelling and testing chaperone activity of small compounds

Gustavo Tiscornia, Erika Lorenzo Vivas, Leslie Matalonga, Ina Berniakovich, Montserrat Barragán Monasterio, Cristina Eguizábal, Laura Gort, Federico González, Carmen Ortiz mellet, José Manuel García Fernández, Antonia Ribes, Anna Veiga, Juan Carlos Izpisua Belmonte*

*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

74 Scopus citations

Fingerprint

Dive into the research topics of 'Neuronopathic Gaucher's disease: Induced pluripotent stem cells for disease modelling and testing chaperone activity of small compounds'. Together they form a unique fingerprint.

Biochemistry, Genetics and Molecular Biology

Medicine and Dentistry

Keyphrases

Immunology and Microbiology